ANPDFSep 254 min readSecond treatment approved by FDA for Niemann-Pick disease, type C: Introducing AQNEURSAFDA approval of AQNEURSA offers new hope for Australian families with Niemann-Pick disease, promising better treatment and quality of life.
ANPDFSep 212 min readA New Hope for NP-C Families: Introducing MiplyffaNew Hope for NP-C Families: Miplyffa, the first FDA-approved treatment for NPC, offers a promising future for our loved ones. Stay informed!
ANPDFSep 161 min readMandos Health Media Release | September 10, 2024Read the letter from Mandos Health here: Here is a summary of the article: INPDA 2023 Meeting : Mandos attended the 2023 INPDA meeting in...
ANPDFSep 61 min readPfrieger's Digest | Issue 11 - March 2024 – July 2024Summaries of latest research advances related to Niemann-Pick diseases, acid sphingomyelinase deficiency (ASMD) and Niemann-Pick type C...
ANPDFSep 41 min readKando Martial Arts Fundraiser: ResultsWe are thrilled to announce the results of our recent fundraiser for Kando Martial Arts! Thanks to the incredible support from our...