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Welcome to the ANPDF blog, where we share the latest updates, stories, and breakthroughs in the fight against Niemann-Pick Disease. Join us as we raise awareness, support families, and drive research forward.

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A New Hope for NP-C Families: Introducing Miplyffa

ANPDF

Sep 212 min read

A New Hope for NP-C Families: Introducing Miplyffa

New Hope for NP-C Families: Miplyffa, the first FDA-approved treatment for NPC, offers a promising future for our loved ones. Stay informed!

105 views

Zevra Therapeutics Media Release | August 2, 2024

ANPDF

Aug 71 min read

Zevra Therapeutics Media Release | August 2, 2024

FDA Advisory Committee Votes Favourably that the Data Support Arimoclomol as Effective Treatment for Patients with NP-C

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Zevra Therapeutics Media Release | March 4, 2024

ANPDF

Mar 51 min read

Zevra Therapeutics Media Release | March 4, 2024

Zevra Therapeutics Provides FDA Update On The PDUFA Action Date For Arimoclomol As A Treatment For Niemann-Pick Disease Type C Read the...

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Zevra Therapeutics Media Release | December 27, 2023

ANPDF

Dec 28, 20231 min read

Zevra Therapeutics Media Release | December 27, 2023

Zevra Therapeutics Announces Resubmission Of Arimoclomol New Drug Application To The U.S. Food And Drug Administration Read the full...

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