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Welcome to the ANPDF blog, where we share the latest updates, stories, and breakthroughs in the fight against Niemann-Pick Disease. Join us as we raise awareness, support families, and drive research forward.

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Azafaros Community Update | December 20, 2024

ANPDF

4 days ago1 min read

Azafaros Community Update | December 20, 2024

Exciting Advances in Azafaros Clinical Programs for NPC and GM Gangliosidoses Today, Azafaros shared an important update about their...

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ANPDF

Jul 171 min read

Azafaros Media Release | July 16, 2024

Azafaros announces positive topline Phase 2 study data with nizubaglustat in GM2 gangliosidosis and Niemann-Pick disease type C Read the...

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ANPDF

Mar 141 min read

Azafaros Media Release | March 12, 2024

Azafaros announces completion of 12-week Phase 2 RAINBOW study evaluating lead asset nizubaglustat in rare disease patients.

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Azafaros Media Release | December 11, 2023

ANPDF

Dec 21, 20231 min read

Azafaros Media Release | December 11, 2023

Azafaros’ Phase 2 RAINBOW study, evaluating nizubaglustat in GM2 and NPC patients, is now fully enrolled Read the full statement from...

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Azafaros Media Releases | January 5-9, 2023

ANPDF

Jan 10, 20231 min read

Azafaros Media Releases | January 5-9, 2023

"Azafaros Receives FDA's IND Clearance and Fast Track Designation for Lead Asset AZ-3102" Read the press release from January 5, 2023...

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