Read the letter from Mandos Health here:
The Mandos Health October 2024 update highlights their progress in Niemann-Pick Type C (NPC) therapies. Key points include a productive FDA meeting on October 10, involving key stakeholders like Dr. Berry-Kravis and Dr. Porter. Mandos also celebrated NPC Awareness Month through community engagement and attended major summits like the NORD Breakthrough Summit. The Expanded Access Program continues to support NPC patients and their families. They remain committed to developing science-driven solutions for NPC.
To join our fight, as well as fund vital research for a cure, support the Australian NPC Disease Foundation in its goals of "Research. Cure. Persevere."
Ways to support NP-C in Australia:
Shop at our online NPC store
Fundraise your way! Check our free resources and inspo online.