Funding research for a cure
This project conducted at The Florey will develop an effective mRNA gene therapy that will significantly improve the health and well-being of those living with NP-C. Findings from this project will enable us to rapidly build an mRNA gene therapy pipeline to treat other genetic disorders, in particular those presenting with childhood dementia.
Key Deliverables
An mRNA gene therapy for Niemann-Pick Disease Type C
Benefit To You
Each year the ANPDF endeavours to raise substantial funds to support this project in the hopes of continuing research for a cure of Niemann-Pick disease type C. This contribution amounts to approximately $75,000 per year.
To support this project, please donate today to give our children a better tomorrow.
Project Details
Research Funding
5 to 10 years
Deadline
Mon Jun 30 2025 02:00:00 GMT+0000 (Coordinated Universal Time)
Project Gallery
