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The Australian NPC Disease Foundation continues to advocate for all research and development programs that present potential treatment options for those living with Niemann-Pick disease (NP-C and ASMD) in Australia.
If you would like to submit your program or have updated information, please contact the Australian NPC Disease Foundation at info@npcd.org.au.
Last updated
October 2024
Program Information and Links:
mRNA gene therapy
The Florey Research Institute of Neuroscience and Mental Health ↪️
Preclinical Stage
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